Huntington’s disease is an obvious target for gene therapies. Caused by long repeats in a single specific gene and the…
Gene Therapies
medically-justified modifications of people
A year ago, we covered preliminary results of ultra-personalized gene therapy for a rare form of Batten disease. Team behind the treatment…
The two eyes communicate not only in disease, but also in response to treatment. David J. Calkins A study on…
A new approach, utilizing lipid vesicles, successfully targeted genes of human papilloma virus (HPV) and completely cured mice from cervical…
Mendelian disorders – although genetically simple – can pose significant challenges in the development of gene therapy. In the case…
Eyes are a popular organ of choice for gene therapies, thanks to their accessibility and limited immune activity. Now, physicians…
Houston’s Methodist Hospital announced a new clinical trial involving genetic modifications. Forty-three women with breast cancer will receive the experimental…
Rare genetic disorder caused by mutations in LAMB2 gene will receive the first gene therapy attempt. The trial started recruitment…
Gene therapy is rarely straightforward mutation correction. The prevalent approach relies on a much simpler procedure of adding just more…
Two patients receiving gene therapy have reported significant improvement in the quality of life. A pilot phase of a clinical…